In this ARC Talks Webinar, Dr. Morie Gertz gave a 101 overview of clinical trials, including consideration in how they are designed, and the phases needed for drug development. Dr. Gertz also discussed current clinical trials that are evaluating the next generation of drugs for the treatment of AL and ATTR amyloidosis.
Original Presentation Date:
May 25, 2023
Key Webinar Highlights:
0:00 — Introduction
3:10 — Start of Dr. Gertz’s presentation
4:30 — The Necessity of Clinical Trials
13:50 — The Phases of Clinical Trials
23:23 — Definition of An Open Label Extension
24:47 — The Study of Vyndaquel for ATTR-CM Patients
26:18 — The Study of Drug Therapies for ATTR-PN/hATTR patients
29:33: — How to Access Clinical Trials
30:35 — Important Clinical Trials Underway
34:00 — Q and A Section
