Category: Clinical Trials
Report From the Amyloidosis Forum Scientific Workshop
The Amyloidosis Forum, a Public Private Partnership with ARC and FDA, hosted the workshop on 22nd January, as part of an ongoing process to develop novel endpoints for clinical trial in AL amyloidosis. In 2020, the Amyloidosis Forum launched a...
First treatment for AL Amyloidosis approved in US
Daratumumab has just been granted approval by the FDA for the treatment of AL Amyloidosis in the United States. Today marks a major milestone and an achievement that has been years in the making. Janssen applied for FDA approval for...
Nobel Prize-Winning Science applied to ATTR Amyloidosis
A groundbreaking study in ATTR amyloidosis, using novel CRISPR/Cas9, has dosed the first patient in the UK. This revolutionary technology brings us a step closer to the dream of curing inherited diseases like hereditary amyloidosis. (more…)
Report from the Amyloidosis Forum’s Initial Meeting at FDA
The inaugural Amyloidosis Forum took place on November 12th, 2019 at FDA’s White Oak Campus in Silver Spring, MD. We could not have hoped for a better turnout, a more spirited and productive discussion. (more…)
Vyndaqel (tafamidis meglumine) and Vyndamax (tafamidis) approved by FDA
This represents the first FDA approved treatment in ATTR-CM for both the wild-type and hereditary forms of ATTR amyloidosis. (more…)